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  • Plenary Session I: Thursday, November 2, 2017

    "Matching Medicines With Mutations"

    Speakers:   Michael P. Boyle, M.D., FCCP and Philip J. Thomas, Ph.D.

    Increasing numbers of people with CF now benefit from disease-altering small molecule therapies that target the basic defect in CFTR.  Use of these therapies has been extended recently using a combination of in vitro laboratory experiments to identify responsive mutations, and clinical trials to determine effect on clinical outcomes. This plenary will summarize how recent advances may allow in the near future over 90% of individuals with CF to benefit from therapies that target the basic defect in CFTR, including even those with the rarest disease causing mutations.

    Topics: Health Outcomes, Treatment, CFTR, Plenary, Clinical Research, Drug Development Pipeline
  • Plenary Session II: Friday, November 3, 2017

    "Lung Transplantation: Challenges & Opportunities for Advanced CF Lung Disease"

    Speakers:  Joseph Pilewski, M.D.

    Plenary 2 will review the progression of CF lung disease and the option of lung transplant to treat advanced disease. The presentation will highlight the challenges associated with each phase of the transplant journey, including the referral to a transplant center, waiting for a transplant, undergoing the transplant procedure, and the care requirements and life after transplant.  

    Topics: Clinical Trials, Plenary, Clinical Research, Drug Development Pipeline
  • Plenary Session I: Thursday, October 27, 2016

    "A Cure for All: Leaving No One Behind"

    Speakers: Mitchell Drumm, Ph.D. and Eric Sorscher, M.D.

    This session describes recent advances toward treatment of cystic fibrosis and the pipeline for new and emerging therapies.

    Topics: Gene Editing, Treatment, Personalized Medicine, Plenary, Drug Development Pipeline
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