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Plenary Session I: Thursday, November 2, 2017
"Matching Medicines With Mutations"
Speakers: Michael P. Boyle, M.D., FCCP and Philip J. Thomas, Ph.D.
Increasing
numbers of people with CF now benefit from disease-altering small molecule
therapies that target the basic defect in CFTR. Use of these therapies
has been extended recently using a combination of in vitro laboratory
experiments to identify responsive mutations, and clinical trials to determine
effect on clinical outcomes. This plenary will summarize how recent advances
may allow in the near future over 90% of individuals with CF to benefit from
therapies that target the basic defect in CFTR, including even those with the
rarest disease causing mutations.
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Plenary Session II: Friday, November 3, 2017
"Lung Transplantation: Challenges & Opportunities for Advanced CF Lung Disease"
Speakers: Joseph Pilewski, M.D.
Plenary 2 will review the
progression of CF lung disease and the option of lung transplant to treat
advanced disease. The presentation will highlight the challenges associated
with each phase of the transplant journey, including the referral to a transplant
center, waiting for a transplant, undergoing the transplant procedure, and the
care requirements and life after transplant.
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Plenary Session I: Thursday, October 27, 2016
"A Cure for All: Leaving No One Behind"
Speakers: Mitchell Drumm, Ph.D. and Eric Sorscher, M.D.
This session describes recent advances toward treatment of cystic fibrosis and the pipeline for new and emerging therapies.