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Plenary Session I: Thursday, November 2, 2017
"Matching Medicines With Mutations"
Speakers: Michael P. Boyle, M.D., FCCP and Philip J. Thomas, Ph.D.
Increasing
numbers of people with CF now benefit from disease-altering small molecule
therapies that target the basic defect in CFTR. Use of these therapies
has been extended recently using a combination of in vitro laboratory
experiments to identify responsive mutations, and clinical trials to determine
effect on clinical outcomes. This plenary will summarize how recent advances
may allow in the near future over 90% of individuals with CF to benefit from
therapies that target the basic defect in CFTR, including even those with the
rarest disease causing mutations.
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Plenary Session II: Friday, November 3, 2017
"Lung Transplantation: Challenges & Opportunities for Advanced CF Lung Disease"
Speakers: Joseph Pilewski, M.D.
Plenary 2 will review the
progression of CF lung disease and the option of lung transplant to treat
advanced disease. The presentation will highlight the challenges associated
with each phase of the transplant journey, including the referral to a transplant
center, waiting for a transplant, undergoing the transplant procedure, and the
care requirements and life after transplant.
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Plenary Session III: Saturday, November 4, 2017
"Partnering With the Community"
Speaker: Drucy Borowitz, M.D. and
Mary B. Dwight
This plenary session will focus on
ways people with CF and their families make a difference by partnering with the
larger community as advocates, by sharing their expertise on living life with
CF with their care center teams, and by supporting with each other through
virtual events and peer mentoring.
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Plenary Session I: Thursday, October 27, 2016
"A Cure for All: Leaving No One Behind"
Speakers: Mitchell Drumm, Ph.D. and Eric Sorscher, M.D.
This session describes recent advances toward treatment of cystic fibrosis and the pipeline for new and emerging therapies.
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Plenary Session II: Friday, October 28, 2016
"Clinical Research: A Worldwide CF Community Effort"
Speakers: Christiane De Boeck, M.D., Ph.D. and Patrick Flume, M.D.
The cystic fibrosis clinical trial pipeline is at present very busy -- and this is great news. This session explains how worldwide collaboration and streamlining can optimize the efficiency in the clinical trial arena.
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Plenary Session III: Saturday, October 29, 2016
"You Can Observe A Lot by Just Watching: Lessons from The CFF Patient Registry"
Speaker: Wayne Morgan, M.D.
This plenary session reviews the role of observational research in improving our understanding of cystic fibrosis, the care of patients with CF, and opportunities to improve this care, highlighting the role of the CF Foundation Patient Registry.